Gene therapy shows promise against blood-clotting disease

A team of gene therapy researchers has reported positive results in a phase 1/2 clinical trial for the inherited bleeding disorder hemophilia B. A single intravenous infusion of a novel bioengineered gene therapy treatment enabled adult participants to safely produce sustained levels of clotting factor that prevented debilitating bleeding episodes. Patients were able to terminate prophylactic treatments—the gene therapy nearly universally eliminated their need for intravenous infusions of manufactured clotting factor.

Gene therapy shows promise against blood-clotting disease

Gene therapy has freed 10 men from nearly all symptoms of hemophilia for a year so far, in a study that fuels hopes that a one-time treatment can give long-lasting help and perhaps even cure ...

Thu 7 Dec 17 from Medical Xpress

Gene therapy shows promise against blood-clotting disease, Wed 6 Dec 17 from AP

Gene therapy shows promise against blood-clotting disease, Wed 6 Dec 17 from AP

Gene therapy shows promise against blood-clotting disease, Wed 6 Dec 17 from AP

One-dose gene therapy produces clotting factor, safely stops bleeding in hemophilia B patients

A team of gene therapy researchers has reported positive results in a phase 1/2 clinical trial for the inherited bleeding disorder hemophilia B. A single intravenous infusion of a novel bioengineered ...

Wed 6 Dec 17 from Medical Xpress

Prophylactic Tx Stems Bleeds in Hemophilia A with Inhibitors (CME/CE)

(MedPage Today) -- HAVEN 2 trial results in pediatric patients called "outstanding and unusual"

Sun 10 Dec 17 from MedPageToday

A 2nd Gene Therapy Breakthrough Against Hemophilia

Coming just days after reports of a gene therapy that pushed the bleeding disorder hemophilia B into remission, new research suggests the same could be true for adults with the "A" form of the ...

Sat 9 Dec 17 from WebMD

First Successful Gene Therapy for Hemophilia A (CME/CE)

(MedPage Today) -- Experts suggest potential cure in sight

Sat 9 Dec 17 from MedPageToday

Gene Therapy May Let Hemophilia Patients Skip Meds

This could eliminate the need for tedious and costly standard treatments, researchers report.

Thu 7 Dec 17 from WebMD

New therapies improve outlook for bleeding and clotting disorders

In three studies being presented today during the 59th American Society of Hematology (ASH) Annual Meeting and Exposition in Atlanta, researchers report remarkable benefits from new, more easily ...

Mon 11 Dec 17 from Eurekalert

Bookmark

Bookmark and Share